Gene therapy proves effective for hemophilia B

Gene therapy proves effective for hemophilia B
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Summary A treatment with gene therapy has been shown to boost output of a vital blood clotting factor.

A single treatment with gene therapy, an experimental technique for fixing faulty genes, has been shown for the first time to boost output of a vital blood clotting factor, possibly offering a long-term solution for people with hemophilia B.Researchers said the same technology was also being studied as a treatment for hemophilia A, the far more common type of the inherited bleeding disorder.
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